drugset / Trial / NCT00144781

A Dose-optimization Study of Aldurazyme® (Laronidase) in Patients With Mucopolysaccharidosis I (MPS I) Disease

NCT00144781

RandomizedParallel-groupOpen-labelTreatment

Summary

The main purpose of this study is to evaluate differences in the pharmacodynamic response of 4 Aldurazyme® (laronidase) dose regimens in patients with Mucopolysaccharidosis I (MPS I).

Timeline

Start
2004-12
Primary completion
2006-01
Completion
2006-01

Drugs

EvaluationDrugModalityDoseRoute
Comparator laronidase Protein / enzyme biologic 0.58 mg/kg
Comparator laronidase Protein / enzyme biologic 1.2 mg/kg
Comparator laronidase Protein / enzyme biologic 1.8 mg/kg