Stem Cell Transplant w/Laronidase for Hurler

Summary

The investigators hypothesize that weekly infusions of Laronidase ERT for 10-12 weeks prior to transplant and 8 weeks following transplant will result in a reduction of glycosaminoglycans (GAG) burden that is associated with decreased complications following transplant.

Timeline

Start

2004-03

Primary completion

2012-11

Completion

2012-11

Drugs

Indications