drugset

drugset / Trial / NCT00244218

Response to Phenylketonuria to Tetrahydrobiopterin (BH4)

NCT00244218 ↗

Phase 1 Terminated 57 enrolled The University of Texas Medical Branch, Galveston

RandomizedSingle-groupTriple-blindTreatment

Summary

The purpose of this study is to determine whether tetrahydrobiopterin (BH4)is effective in treating patients with PKU.

Timeline

Start: 2005-04
Primary completion: 2009-03
Completion: 2015-01

Drugs

Evaluation	Drug	Modality	Dose	Route
Subject	sapropterin	Unknown	10 mg/kg	Oral

Indications