drugset / Trial / NCT00260000
Study of BH4, a New and Simple Treatment of Mild PKU
Phase 2
Completed
15 enrolled
The Kennedy Institute-National Eye Clinic
Sygekassernes Helsefond · collab
Non-randomizedSingle-groupOpen-labelTreatment
Summary
The main purpose is to test whether treatment with BH4-tablets can replace the protein restrictive diet in patients with mild PKU caused by a certain frequent mutation.
Timeline
- Start
- 2005-04
- Primary completion
- —
- Completion
- 2005-12
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | 5,6,7,8-tetrahydrobiopterin | Unknown | — | Oral |