drugset / Trial / NCT00433147

A Study of AT2101 (Afegostat Tartrate) in Adult Patients With Type 1 Gaucher Disease Currently Receiving Enzyme Replacement Therapy

NCT00433147 ↗

Phase 2 Completed 30 enrolled Amicus Therapeutics
RandomizedParallel-groupOpen-labelTreatment

Summary

This study was conducted to test the safety and tolerability of afegostat tartrate in participants with type 1 Gaucher disease already receiving enzyme replacement therapy.

Timeline

Start
2007-03-23
Primary completion
2008-02-19
Completion
2008-02-19

Drugs

EvaluationDrugModalityDoseRoute
Subject Afegostat Other / unclassified 25 mg Oral
Subject Afegostat Other / unclassified 150 mg Oral