drugset / Trial / NCT00438789

The Paroxysmal Nocturnal Hemoglobinuria Early Access Treatment Protocol

NCT00438789 ↗

Expanded access Approved for marketing Alexion Pharmaceuticals, Inc.

Summary

The primary objective is to provide access to eculizumab for PNH patient pending commercial availability.

Timeline

Start
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Primary completion
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Completion
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Drugs

EvaluationDrugModalityDoseRoute
Subject Eculizumab Monoclonal antibody 600 mg Intravenous
Subject Eculizumab Monoclonal antibody 900 mg Intravenous