drugset / Trial / NCT00526071

Open-label Long-term Safety Study of AT1001 (Migalastat Hydrochloride) in Participants With Fabry Disease Who Have Completed a Previous AT1001 Study

NCT00526071

Phase 2 Terminated 23 enrolled Amicus Therapeutics
NaSingle-groupOpen-labelTreatment

Summary

Study to evaluate the long-term safety, tolerability, and pharmacodynamics (PD) of migalastat hydrochloride (HCl) (migalastat) in participants with Fabry disease

Timeline

Start
2007-09-17
Primary completion
2012-09-08
Completion
2012-09-08

Drugs

EvaluationDrugModalityDoseRoute
Subject migalastat Other / unclassified 150 mg Oral

Indications