drugset / Trial / NCT00634660

Safety and Tolerability Study of rAvPAL-PEG to Treat Phenylketonuria

NCT00634660

Phase 1 Completed 25 enrolled BioMarin Pharmaceutical
RandomizedParallel-groupOpen-labelTreatment

Summary

The purpose of this study is to assess the safety and tolerability of injections of rAvPAL-PEG in subjects with PKU.

Timeline

Start
2008-05
Primary completion
2009-04
Completion
2009-10

Drugs

EvaluationDrugModalityDoseRoute
Comparator Pegvaliase Protein / enzyme biologic 0.001 mg/kg Subcutaneous
Comparator Pegvaliase Protein / enzyme biologic 0.003 mg/kg Subcutaneous
Comparator Pegvaliase Protein / enzyme biologic 0.01 mg/kg Subcutaneous
Comparator Pegvaliase Protein / enzyme biologic 0.03 mg/kg Subcutaneous
Comparator Pegvaliase Protein / enzyme biologic 0.1 mg/kg Subcutaneous
Comparator Pegvaliase Protein / enzyme biologic 0.3 mg/kg Subcutaneous
Comparator Pegvaliase Protein / enzyme biologic 1 mg/kg Subcutaneous

Indications