Once-A-Day Prophylaxis for Youth and Young Adults With Severe Hemophilia A

Summary

The primary objective of this study is to test the feasibility of a large-scale clinical trial of once-daily prophylaxis. The secondary objectives are to collect clinical efficacy outcomes so that we can better plan a large-scale study; we will estimate the effect size and variability of effect and resource utilization of once-daily prophylaxis to allow us to set a sample size for a definitive trial.

Timeline

Start

2008-07

Primary completion

2011-04

Completion

2011-04

Drugs

Indications