Human Heterologous Liver Cells for Infusion in Children With Urea Cycle Disorders

Summary

Urea cycle disorders are rare inherited diseases that generally have a poor outcome. In this study, neonates and infants with UCD will be included within the first 3 months of life and will be treated by repetitive application of human liver cells to reduce the risk of neurological deterioration while awaiting OLT.

Timeline

Start

2008-07

Primary completion

2015-11

Completion

2015-11

Drugs

Indications