drugset
drugset / Trial / NCT01005004

Study of Human Central Nervous System (CNS) Stem Cells Transplantation in Pelizaeus-Merzbacher Disease (PMD) Subjects

NCT01005004 ↗

Phase 1 Completed 4 enrolled StemCells, Inc.
NaSingle-groupOpen-label

Summary

The purpose of this study is to determine the safety and preliminary effectiveness of human central nervous system stem cells (HuCNS-SC®) transplantation in patients with Connatal Pelizaeus-Merzbacher Disease (PMD).

Timeline

Start
2009-11
Primary completion
2012-10
Completion
2012-12

Drugs

EvaluationDrugModalityDoseRoute
Subject Rexlemestrocel-L Cell therapy — Other

Indications

Pelizaeus-Merzbacher disease, connatal form