Human Heterologous Liver Cells for Infusion in Children With Urea Cycle Disorders

Summary

Treatment with liver cell infusion for children with urea cycle disorders (UCD).

Timeline

Start

2010-12

Primary completion

2015-12

Completion

2015-12

Publications

• Background Meyburg J, Das AM, Hoerster F, Lindner M, Kriegbaum H, Engelmann G, Schmidt J, Ott M, Pettenazzo A, Luecke T, Bertram H, Hoffmann GF, Burlina A. One liver for four children: first clinical series of liver cell transplantation for severe neonatal urea cycle defects. Transplantation. 2009 Mar 15;87(5):636-41. doi: 10.1097/TP.0b013e318199936a.

Drugs

Indications