drugset / Trial / NCT01388764

Safety, Tolerability and Effects of L-Arginine in Boys With Dystrophinopathy on Corticosteroids

NCT01388764

Phase 1 Completed 7 enrolled Massachusetts General Hospital
Non-randomizedSingle-groupOpen-label

Summary

The purpose of the study is to assess the safety, tolerability, and effects of L-Arginine on muscles in boys with dystrophinopathy on corticosteroids. Specifically, to see if L-arginine reduces muscle signal abnormalities on MRI done pre and post 30 days of L-arginine administration.

Timeline

Start
2012-01
Primary completion
2012-05
Completion
2012-05

Drugs

EvaluationDrugModalityDoseRoute
Subject L-arginine Small molecule 0.3 g/kg Oral