drugset / Trial / NCT01541397
Bone Mineral Density in Adults With Hyperphenylalaninemia on Kuvan Therapy
Terminated
6 enrolled
The University of Texas Health Science Center, Houston
BioMarin Pharmaceutical · collab
Non-randomizedSingle-groupOpen-labelTreatment
Summary
Prospective study to compare the bone mineral density in adults with HPA on KUVAN™ therapy to those not on therapy. The investigators hypothesize that after one year of KUVAN™ therapy, there will be an improvement in their bone mineral density.
Timeline
- Start
- 2011-06
- Primary completion
- 2012-08
- Completion
- 2012-08
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | sapropterin | Unknown | 20 mg/kg | Oral |