Short and Long Term Treatment With 4-AP in Ambulatory SMA Patients

Summary

The purpose of this study is to assess whether 4-AP (Dalfampridine-ER, Ampyra) improves walking ability and endurance in adult patients with Spinal muscular atrophy (SMA) Type 3 compared to placebo and whether the duration of treatment affects outcome.

Timeline

Start

2012-06-01

Primary completion

2015-09

Completion

2015-09

Drugs

Indications