drugset / Trial / NCT01671111

Study for Transfusionally Iron Overloaded Children, Adolescents and Adults Using FBS0701 (SSP-004184)

NCT01671111

Phase 2 Terminated 30 enrolled Shire
NaSingle-groupOpen-labelTreatment

Summary

The purpose of this extension study is to evaluate SSP-004184AQ in patients with transfusional iron overload and to provide data on long term safety and efficacy. SSP-004184AQ is an iron chelator under development for chronic daily oral administration to patients with transfusional iron overload

Timeline

Start
2012-08-14
Primary completion
2014-04-24
Completion
2014-04-24

Drugs

EvaluationDrugModalityDoseRoute
Subject SPD602 Unknown 8 mg/kg Oral
Subject SPD602 Unknown 75 mg/kg Oral

Indications