drugset / Trial / NCT01681940
Long-term Efficacy and Safety of Lamazym for the Treatment of Patients With Alpha-Mannosidosis
NaSingle-groupOpen-labelTreatment
Summary
The overall objective is to evaluate the long-term efficacy, safety and tolerability of repeated Lamazym i.v. treatment in patients 5-21 years of age with alpha-Mannosidosis
Timeline
- Start
- 2012-01
- Primary completion
- 2012-08
- Completion
- 2013-09
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | Velmanase Alfa | Protein / enzyme biologic | 1 mg/kg | Intravenous |