drugset / Trial / NCT01784718

Buphenyl Therapy for Byler's Disease

NCT01784718

Expanded access No longer available University of Pittsburgh

Summary

This is a single patient compassionate use protocol to determine whether Buphenyl (4-phenylbutyrate) will improve the poor bile flow associated with Byler Disease.

Timeline

Start
Primary completion
Completion

Drugs

EvaluationDrugModalityDoseRoute
Subject Sodium Phenylbutyrate Small molecule