drugset / Trial / NCT01797276
Dichloroacetate Treatment of Congenital Lactic Acidosis Phase B: Expanded Access
Summary
Expanded access to DCA as continued treatment for congenital lactic acidosis.
Timeline
- Start
- —
- Primary completion
- —
- Completion
- —
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | Dichloroacetate | Small molecule | 25 mg/kg | — |