Phase 2 Study of EPI-743 for Treatment of Rett Syndrome

Summary

Rett syndrome is a severe neurodevelopmental disorder that primarily affects female children. Rett syndrome is characterized by significant elevation in blood markers of oxidative stress. EPI-743 is a novel therapeutic with demonstrated efficacy and safety in the treatment of disorders characterized by oxidative stress. The purpose of this study is to examine the safety and efficacy of EPI-743 in a population of children with Rett syndrome.

Timeline

Start

2013-01

Primary completion

2013-12

Completion

2014-01

Drugs

Indications