drugset / Trial / NCT02292186

A Extension Study to Evaluate Revusiran (ALN-TTRSC) in Patients With Transthyretin (TTR) Cardiac Amyloidosis

NCT02292186 ↗

Phase 2 Completed 25 enrolled Alnylam Pharmaceuticals
NaSingle-groupOpen-labelTreatment

Summary

The purpose of this study was to evaluate the safety and clinical activity of long-term dosing with revusiran (ALN-TTRSC). Dosing has been discontinued; patients are being followed-up for safety.

Timeline

Start
2014-10
Primary completion
2017-02-22
Completion
2017-02-22

Drugs

EvaluationDrugModalityDoseRoute
Subject Revusiran Small interfering RNA (siRNA) — —

Indications

No indication recorded.