drugset / Trial / NCT02405598
Evaluation of Salbutamol as an Adjuvant Therapy for Pompe Disease
NaSingle-groupOpen-labelTreatment
Summary
evaluate if beta 2-adrenergic agonist can have adjuvant effect to patients with infantile-onset Pompe disease under enzyme replacement therapy
Timeline
- Start
- 2013-10
- Primary completion
- 2015-07
- Completion
- 2016-06
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | Salbutamol | Unknown | 0.2 mg/kg | — |
| Subject | Salbutamol | Unknown | 4 mg | — |
| Subject | Salbutamol | Unknown | 8 mg | — |