drugset / Trial / NCT02520934
Miglustat on Gaucher Disease Type IIIB
Non-randomizedParallel-groupOpen-labelTreatment
Summary
evaluate the combination therapy with Miglustat and enzyme replacement therapy (ERT) on Gaucher disease
Timeline
- Start
- 2015-07
- Primary completion
- 2017-12
- Completion
- 2019-12
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | Miglustat | Small molecule | — | — |