Safety, Tolerability and Effect of ARC-AAT Injection on Circulating and Intrahepatic Alpha-1 Antitrypsin Levels

Summary

Patients with Alpha-1 Antitrypsin Deficiency (AATD) will be enrolled to receive multiple doses of ARC-AAT Injection. All subjects will require a pre-dose biopsy and a biopsy post last dose.

Timeline

Start

2016-10

Primary completion

2016-11

Completion

2016-11

Outcome

Outcome not reported

Stopped: “Company decision to not initiate trial”

Drugs

Indications