drugset / Trial / NCT02998879
Trial on Safety and Efficacy of Velmanase Alfa Treatment in Pediatric Patients With Alpha-Mannosidosis
NaSingle-groupOpen-labelTreatment
Summary
The main objectives of the study are to evaluate safety and efficacy of repeated treatment with recombinant human alfa-mannosidase of patients with alfa-mannosidosis aged less than 6 years
Timeline
- Start
- 2016-12
- Primary completion
- 2020-07
- Completion
- 2020-07
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | Velmanase Alfa | Protein / enzyme biologic | 1 mg/kg | Intravenous |