drugset / Trial / NCT03184584
Open-Label Rollover Study of PBI 4050 in Subjects With Alström Syndrome
NaSingle-groupOpen-labelTreatment
Summary
Phase 2, open-label, single-arm, multi-centre study evaluating the long term safety and tolerability of PBI-4050 in subjects with Alström Syndrome who have completed a preceding ProMetic-sponsored Alström Syndrome study with PBI-4050.
Timeline
- Start
- 2017-10-09
- Primary completion
- 2020-05-08
- Completion
- 2020-05-08
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | SETOGEPRAM | Small molecule | 800 mg | Oral |