drugset / Trial / NCT03386214

Pevonedistat in Combination With Ruxolitinib for Treatment of Patients With Myelofibrosis

NCT03386214

Non-randomizedSequentialOpen-labelTreatment

Summary

Based on the investigators' preclinical data, the combination of pevonedistat and ruxolitinib may provide greater clinical responses in patients with myelofibrosis compared to ruxolitinib monotherapy via inhibition of NFκB in addition to JAK-STAT signaling.

Timeline

Start
2018-04-23
Primary completion
2021-09-12
Completion
2021-10-04

Drugs

EvaluationDrugModalityDoseRoute
Subject Pevonedistat Small molecule 5 mg/m2 Intravenous
Subject Pevonedistat Small molecule 10 mg/m2 Intravenous
Subject Pevonedistat Small molecule 20 mg/m2 Intravenous
Background Ruxolitinib Small molecule

Indications