drugset / Trial / NCT03400098

ATTR Expanded Access Program (EAP) by Ionis

NCT03400098 ↗

Expanded access Approved for marketing Ionis Pharmaceuticals, Inc.

Summary

The purpose of this program is to provide expanded access to Inotersen for up to 100 Patients with Hereditary Transthyretin Amyloidosis (hTTR).

Timeline

Start
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Primary completion
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Completion
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Drugs

EvaluationDrugModalityDoseRoute
Subject Inotersen Antisense oligonucleotide — Subcutaneous