drugset / Trial / NCT03404856

Study of ORL-1G (D-galactose) in Patients With Glycogen Storage Disease Type 14

NCT03404856 ↗

Phase 1/2 Unknown 5 enrolled Orpha Labs
NaSingle-groupOpen-labelTreatment

Summary

Study of ORL-1G in Patients With Glycogen Storage Disease Type 14

Timeline

Start
2017-10-31
Primary completion
2019-10-31
Completion
2019-10-31

Drugs

EvaluationDrugModalityDoseRoute
Subject ORL-1G Unknown — Oral