Expanded Access Use of Itacitinib to Treat a Single Patient With Aplastic Anemia

Summary

Expanded Access Use of Itacitinib to Treat a Single Patient With Aplastic Anemia

Timeline

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Primary completion

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Completion

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Publications

• Rosenberg JM, Peters JM, Hughes T, Lareau CA, Ludwig LS, Massoth LR, Austin-Tse C, Rehm HL, Bryson B, Chen YB, Regev A, Shalek AK, Fortune SM, Sykes DB. JAK inhibition in a patient with a STAT1 gain-of-function variant reveals STAT1 dysregulation as a common feature of aplastic anemia. Med. 2022 Jan 14;3(1):42-57.e5. doi: 10.1016/j.medj.2021.12.003.

Drugs

Indications