drugset / Trial / NCT03961243
Lentiviral FIX Gene Therapy
Non-randomizedSingle-groupOpen-labelTreatment
Summary
This study is a Phase I trial using an advanced lentiviral vector to deliver a functional gene for human clotting factor IX into patients with hemophilia B, to evaluate the safety and efficacy of infusion of lentiviral gene modified autologous stem cells in patients.
Timeline
- Start
- 2025-06-01
- Primary completion
- 2027-05-31
- Completion
- 2028-06-01
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | YUVA-GT-F901 | Unknown | — | — |