drugset / Trial / NCT04020055

A Study to Evaluate Migalastat in Fabry Subjects With Amenable GLA Variant and Renal Disease

NCT04020055

Phase 3 Active not recruiting 14 enrolled Amicus Therapeutics
Non-randomizedParallel-groupOpen-labelTreatment

Summary

An Open-label Study to Evaluate the Safety and Pharmacokinetics of Migalastat HCl in Subjects with Fabry Disease and Amenable GLA Variants and Severe Renal Impairment (SRI) or End Stage Renal Disease (ESRD)

Timeline

Start
2022-10-31
Primary completion
2026-12-31
Completion
2026-12-31

Drugs

EvaluationDrugModalityDoseRoute
Subject migalastat Other / unclassified 150 mg Oral

Indications