drugset / Trial / NCT04092205

Phase 2a Pilot Study of NBMI Treatment in Patients With Beta Thalassemia Major, Requiring Iron Chelation

NCT04092205 ↗

Phase 2 Completed 13 enrolled EmeraMed
NaSingle-groupOpen-labelTreatment

Summary

A pilot study to explore safety and efficacy of NBMI treatment in patients with Beta Thalassemia Major requiring iron chelation Investigational product: NBMI (N1,N3-bis(2-mercaptoethyl) isophthalamide), INN: Emeramide Indication: Beta Thalassemia Major

Timeline

Start
2019-11-21
Primary completion
2020-07-30
Completion
2020-08-30

Drugs

EvaluationDrugModalityDoseRoute
Subject Emeramide Small molecule 600 mg —