Phase II Clinical Trial of Clenbuterol in Adult Patients With Pompe Disease

Summary

The goals of this study are to determine safety and efficacy with regard to motor function of oral clenbuterol in combination with ERT in subjects with LOPD

Timeline

Start

2023-01-01

Primary completion

2025-06-30

Completion

2025-12-30

Outcome

Outcome not reported

Stopped (Business): “hasn't got the funding”

Drugs

Indications