drugset / Trial / NCT04094948

Phase II Clinical Trial of Clenbuterol in Adult Patients With Pompe Disease

NCT04094948

Phase 2 Withdrawn Duke University
RandomizedParallel-groupQuadruple-blindTreatment

Summary

The goals of this study are to determine safety and efficacy with regard to motor function of oral clenbuterol in combination with ERT in subjects with LOPD

Timeline

Start
2023-01-01
Primary completion
2025-06-30
Completion
2025-12-30

Drugs

EvaluationDrugModalityDoseRoute
Subject Clenbuterol Small molecule 80 ug Oral