Study Evaluating Patients With Cystinuria and Efficacy and Safety Exploratory Study in the Youngest Children

Summary

This is a multicenter, randomized, controlled versus placebo, double-blinded, 4 parallel arms, dose-ranging main study, to evaluate the efficacy, safety and tolerability, and acceptability of repeated doses of ADV7103, after 7 days of treatment, in patients with cystinuria, and an efficacy and safety exploratory study in the youngest children.

Timeline

Start

2024-03-01

Primary completion

2025-05-01

Completion

2025-06-01

Outcome

Outcome not reported

Stopped (Business): “Unspecified business decision/strategic reason”

Drugs

Indications