drugset / Trial / NCT04195399

A Study of a New Drug, Nirogacestat, for Treating Desmoid Tumors That Cannot be Removed by Surgery

NCT04195399

NaSingle-groupOpen-labelTreatment

Summary

This phase II trial studies the side effects and how well nirogacestat works in treating patients less than 18 years of age with desmoid tumors that has grown after at least one form of treatment by mouth or in the vein that cannot be removed by surgery. Nirogacestat may stop the growth of tumor cells by blocking some of the enzymes needed for cell growth.

Timeline

Start
2020-10-07
Primary completion
2026-03-31
Completion
2027-04-10

Drugs

EvaluationDrugModalityDoseRoute
Subject Nirogacestat Small molecule Oral

Indications