drugset / Trial / NCT04327973

Expanded Access for ATB200/AT2221 for the Treatment of IOPD

NCT04327973

Expanded access Available Amicus Therapeutics

Summary

This is an expanded access program (EAP) for eligible participants designed to provide access to ATB200/AT2221.

Timeline

Start
Primary completion
Completion

Drugs

EvaluationDrugModalityDoseRoute
Background Cipaglucosidase alfa Protein / enzyme biologic
Background Miglustat Small molecule