drugset
drugset / Trial / NCT04531878

BSEP Function Rescue During Childhood Inhereditary Cholestatic Diseases

NCT04531878 ↗

Phase 2/3 Withdrawn Children's Hospital of Fudan University
NaSingle-groupOpen-labelTreatment

Summary

The purpose of the study is to improve the prognosis of inhereditary cholestasis caused by ABCB11 gene mutations by using BSEP function rescue drugs

Timeline

Start
2023-02-08
Primary completion
2023-02-08
Completion
2023-02-08

Outcome

Outcome not reported

Stopped (Business): “lack of funding”

Drugs

EvaluationDrugModalityDoseRoute
Subject 4-Phenylbutyrate Unknown 500 mg/kg Oral

Indications

intrahepatic cholestasis