drugset / Trial / NCT04720261

Efficacy of a Personalized Caplacizumab Regimen Based on ADAMTS13 Activity Monitoring in Adult aTTP

NCT04720261

Phase 2 Terminated 58 enrolled University Hospital, Rouen
NaSingle-groupOpen-labelTreatment

Summary

The aim of the study is to evaluate the efficacy of a personalized caplacizumab regimen based on ADAMTS13 activity monitoring in adult acquired thrombotic thrombocytopenic purpura (aTTP): This study is a phase II, prospective, multicenter non-inferiority single-arm study.

Timeline

Start
2021-04-26
Primary completion
2023-05-16
Completion
2023-05-16

Drugs

EvaluationDrugModalityDoseRoute
Subject Caplacizumab Protein / enzyme biologic