drugset / Trial / NCT04728217
Health Related Quality of Life of Youth and Young Adults With Haemophilia A
NaSingle-groupOpen-labelPrevention
Summary
Research question: Whether there are the changes in quality of life in patients with haemophilia A after switching from SHL FVIII prophylaxis to efmoroctocog alfa prophylaxis? A 12-month prospective open-label, single-arm multicentre study. Evaluation of parameters will be carried out on the backdrop of patient treatment in the settings of routine medical practice. No medical examinations/ procedures/ treatment(s) on the top of regular medical practice are planned, except fixed time of examinations.
Timeline
- Start
- 2021-04-15
- Primary completion
- 2023-02-20
- Completion
- 2023-02-20
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | Efmoroctocog Alfa | Protein / enzyme biologic | 50 iu/kg | — |