drugset / Trial / NCT04794101
Follow-up Gene Therapy Trial for the Treatment of X-linked Retinitis Pigmentosa Associated With Variants in the RPGR Gene
RandomizedParallel-groupSingle-blindTreatment
Summary
A clinical trial of AAV5-hRKp.RPGR vector for participants with X-linked retinitis pigmentosa (XLRP)
Timeline
- Start
- 2020-12-04
- Primary completion
- 2029-09-20
- Completion
- 2029-12-07
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | AAV5-hRKp.RPGR | Gene therapy (AAV / viral vector) | — | Subcutaneous |