drugset / Trial / NCT04919473
Dose-Escalation Study to Evaluate the Safety and Tolerability of Intravitreal vMCO-I in Patients With Advanced Retinitis Pigmentosa
Non-randomizedSequentialOpen-labelTreatment
Summary
The purpose of the study is to evaluate the safety and tolerability of a single intravitreal injection of virally-carried Multi-Characteristic Opsin I (vMCO-I)
Timeline
- Start
- 2019-10-23
- Primary completion
- 2020-02-25
- Completion
- 2020-10-31
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | vMCO-I | Gene therapy (AAV / viral vector) | 1.75e+11 vg | Intravitreal |
| Subject | vMCO-I | Gene therapy (AAV / viral vector) | 3.5e+11 vg | Intravitreal |