drugset / Trial / NCT05116787

BCX9930 for the Treatment of Paroxysmal Nocturnal Hemoglobinuria (PNH) in Participants Not Receiving Other Complement Inhibitor Therapy

NCT05116787

Phase 2 Terminated 12 enrolled BioCryst Pharmaceuticals
RandomizedParallel-groupDouble-blindTreatment

Summary

The purpose of this study was to determine the efficacy and safety of BCX9930 monotherapy for the treatment of adult participants with PNH not currently receiving complement inhibitor therapy.

Timeline

Start
2021-10-26
Primary completion
2023-09-18
Completion
2023-09-18

Drugs

EvaluationDrugModalityDoseRoute
Subject BCX9930 Unknown 400 mg Oral
Subject BCX9930 Unknown 500 mg Oral