drugset / Trial / NCT05130437
A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
NaSingle-groupOpen-labelTreatment
Summary
The main purpose of this study is to evaluate the long-term safety of mRNA-3927 administered to participants with propionic acidemia (PA) who have previously participated in Study mRNA-3927-P101 (NCT04159103).
Timeline
- Start
- 2021-11-09
- Primary completion
- 2029-12-04
- Completion
- 2031-12-04
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | mRNA-3927 | Messenger RNA (mRNA) | — | Intravenous |