drugset / Trial / NCT05152732
Safety and Tolerability of VGB-R04 in Patients With Haemophilia B
NaSingle-groupOpen-labelTreatment
Summary
An Open-Label, Non-Randomized, uncontrolled, single-dose pilot study of VGB-R04 in subjects with Hemophilia B.
Timeline
- Start
- 2021-12-28
- Primary completion
- 2025-03
- Completion
- 2025-12
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | VGB-R04 | Gene therapy (AAV / viral vector) | — | Intravenous |