drugset / Trial / NCT05158296

Study to Evaluate the Efficacy Safety and Tolerability of Ultevursen in Subjects With RP Due to Mutations in Exon 13 of the USH2A Gene (Sirius)

NCT05158296 ↗

Phase 2/3 Terminated 7 enrolled Laboratoires Thea Sepul Bio · collab
RandomizedParallel-groupQuadruple-blindTreatment

Summary

The purpose of this study is to evaluate the efficacy safety and tolerability of ultevursen administered via intravitreal injection (IVT) in subjects with Retinitis Pigmentosa (RP) due to mutations in exon 13 of the USH2A gene.

Timeline

Start
2021-12-08
Primary completion
2022-10-12
Completion
2022-10-12

Outcome

Outcome not reported

Stopped (Business): “Business decision”

Drugs

EvaluationDrugModalityDoseRoute
Subject Ultevursen Antisense oligonucleotide 60 ug Intravitreal