drugset / Trial / NCT05399069
Safety and Tolerability of VGR-R01 in Patients With Bietti Crystalline Dystrophy
NaSingle-groupOpen-labelTreatment
Summary
An Open-Label, Non-Randomized, Uncontrolled, Single-dose Pilot Study of VGR-R01 in Patients with Bietti Crystalline Dystrophy.
Timeline
- Start
- 2022-09-15
- Primary completion
- 2024-05
- Completion
- 2024-05
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | VGR-R01 | Gene therapy (AAV / viral vector) | — | Other |