drugset / Trial / NCT05402332
Evaluating the Efficacy and Safety of D-galactose in PGM1-CDG (AVTX-801)
Phase 2
Not yet recruiting
8 enrolled
Eva Morava-Kozicz
Children's Hospital of Philadelphia · collab
RandomizedCrossoverTriple-blindTreatment
Summary
This is a clinical trial to evaluate the efficacy of AVTX-801 (D-galactose) on the clinical manifestations of PGM1-CDG in participants currently taking D-galactose.
Timeline
- Start
- 2026-10-01
- Primary completion
- 2028-03-02
- Completion
- 2028-03-02
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | Galactose | Diagnostic / imaging agent | 1.5 g/kg | — |