drugset / Trial / NCT05432466

Clinical Trial to Compare the Efficacy of Celiprolol to Placebo in Patients With Vascular Ehlers-Danlos Syndrome

NCT05432466

Phase 3 Recruiting 150 enrolled Acer Therapeutics Inc.
RandomizedParallel-groupQuadruple-blindTreatment

Summary

This is a prospective, Phase 3, randomized, double-blind, placebo-controlled efficacy study to evaluate celiprolol in patients genetically confirmed as COL3A1-positive vEDS using a decentralized clinical trial design.

Timeline

Start
2022-11-07
Primary completion
2029-03-01
Completion
2029-04-01

Drugs

EvaluationDrugModalityDoseRoute
Subject Celiprolol Small molecule 200 mg Oral