drugset / Trial / NCT05441553
A Study to Evaluate the Safety and Efficacy of VGB-R04 in Adult Hemophilia B Patients
NaSingle-groupOpen-labelTreatment
Summary
A multicenter, open, non-randomized, phase I/II, two-phase clinical study. The dose exploration phase was phase I, and the dose extension phase was phase II.
Timeline
- Start
- 2022-07
- Primary completion
- 2025-01
- Completion
- 2025-01
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Subject | VGB-R04 | Gene therapy (AAV / viral vector) | — | Intravenous |